TEL AVIV, Israel, May 26, 2017 (GLOBE NEWSWIRE) -- Bioblast Pharma Ltd. (Nasdaq:ORPN), a clinical-stage, orphan
disease-focused biotechnology company, today announced financial results for the first quarter ended March 31, 2017.
First Quarter 2017 Financial Results and Cash Position
- R&D Expenses: Research and development expenses were $1.1 million for the quarter ended March 31, 2017,
compared to $1.9 million for the same period in 2016. The decrease was primarily related to reduced clinical trial related
activities, specifically as our planned Phase 2b clinical study in Ocular Pharyngeal Muscular Dystrophy (OPMD) patients has not
yet been initiated; the decrease in costs was slightly offset by increased preclinical activities related to required toxicity
studies.
- Pre-Commercial Expenses: Pre-commercial expenses were $0.4 million for the quarter ended March 31, 2017,
compared to $0.8 million for the same period in 2016.
- G&A Expenses: General and administrative expenses were $1.1 million for the quarter ended March 31,
2017, compared to $1.9 million for the same period in 2016. The decrease was primarily related to downsizing of the management
team, which took effect primarily in the second quarter of 2016, offset by costs related to a terminated securities offering
announced on April 6, 2017.
- Net Loss: For the quarter ended March 31, 2017, net loss attributable to holders of ordinary shares was
($2.7) million, or ($0.16) per basic and diluted share, as compared to a net loss of ($4.6) million, or ($0.32) per share, for
the same period in 2016.
- Cash Position: Cash, cash equivalents and short-term bank deposits as of March 31, 2017, were $7.1 million,
compared to $9.9 million as of December 31, 2016, primarily reflecting our first quarter operating expenditures. Additional
funding beyond our existing cash resources will be required to entirely cover the cost of the Phase 2b clinical study and the
underlying expenses of our operations while the study is ongoing. Should we be unable to obtain the additional funding required
to continue our clinical activity, we may need to reduce our activities and to explore strategic alternatives until we have
sufficient resources.
About Bioblast
Bioblast Pharma is a clinical-stage biotechnology company committed to developing clinically meaningful
therapies for patients with rare and ultra-rare genetic diseases with a lead drug candidate, trehalose 90mg/mL solution, in Phase 2
development. Bioblast was founded in 2012 and is traded on the NASDAQ under the symbol “ORPN.” For more information, please
visit our website, www.BioblastPharma.com, the content of which is not incorporated herein by reference.
Forward Looking Statements
This press release contains forward-looking statements within the meaning of the "safe harbor" provisions of the
Private Securities Litigation Reform Act of 1995 and other Federal securities laws. For example, we are using forward looking
statements when we discuss plans to conduct a Phase 2b clinical study, the design and timing of such study, and the company’s
expected need for additional funding or possible need to reduce activities or pursue other alternatives. In addition, historic
results of scientific research and clinical and preclinical trials do not guarantee that the conclusions of future research or
trials will suggest similar conclusions or those historic results referred to in this press release will be interpreted in a
similar way in light of additional research and clinical and preclinical trial results. Any forward-looking statements in this
press release are based on management’s current expectations of future events and are subject to a number of risks and
uncertainties that could cause actual results to differ materially and adversely from those set forth in or implied by such
forward-looking statements. Because such statements deal with future events and are based on Bioblast Pharma Ltd.'s current
expectations, they are subject to various risks and uncertainties and actual results, performance or achievements of Bioblast
Pharma could differ materially from those described in or implied by the statements in this press release, including those
discussed under the heading "Risk Factors" in Bioblast Pharma's Annual Report on Form 20-F filed with the Securities and Exchange
Commission ("SEC") on February 24, 2017, and in any subsequent filings with the SEC. Except as otherwise required by law, Bioblast
Pharma disclaims any intention or obligation to update or revise any forward-looking statements, which speak only as of the date
hereof, whether as a result of new information, future events or circumstances or otherwise.
| |
| Bioblast Pharma Ltd. |
| |
| Consolidated Statement of Operations |
| |
| (U.S. dollars in thousands, except share and per share
amounts) |
| |
| |
Three Months Ended |
| |
March
31
|
| |
|
2017 |
|
|
|
2016 |
|
| |
(Unaudited) |
|
(Unaudited) |
| |
|
|
|
| Research and development |
$ |
1,099 |
|
|
$ |
1,858 |
|
| Pre-commercialization |
|
406 |
|
|
|
772 |
|
| General and administrative |
|
1,135 |
|
|
|
1,862 |
|
| Total
operating expenses |
|
2,640 |
|
|
|
4,492 |
|
| Loss from operations |
|
(2,640 |
) |
|
|
(4,492 |
) |
| |
|
|
|
| Financial income, net |
|
8 |
|
|
|
27 |
|
| |
|
|
|
| Loss before taxes on income |
|
(2,632 |
) |
|
|
(4,465 |
) |
| |
|
|
|
| Taxes on income |
|
40 |
|
|
|
129 |
|
| |
|
|
|
| Net loss |
$ |
(2,672 |
) |
|
$ |
(4,594 |
) |
| |
|
|
|
| Net loss attributable to Ordinary shareholders |
$ |
(2,672 |
) |
|
$ |
(4,594 |
) |
| |
|
|
|
| Net loss per share attributable to Ordinary shareholders - basic and diluted |
$ |
(0.16 |
) |
|
$ |
(0.32 |
) |
| |
|
|
|
| Weighted average number of Ordinary shares outstanding - basic and diluted |
|
16,391,770 |
|
|
|
14,467,984 |
|
| |
|
|
|
| Bioblast Pharma Ltd. |
| |
| Consolidated Balance Sheet Data |
| |
| (U.S. dollars in thousands, except share amounts) |
| |
| |
March 31, 2017 |
|
December 31, 2016 |
| |
(Unaudited) |
|
(Audited) |
| ASSETS |
|
|
|
| CURRENT ASSETS: |
|
|
|
| Cash and cash equivalents |
$ |
4,100 |
|
|
$ |
6,871 |
|
| Short-term bank deposits |
|
3,017 |
|
|
|
3,007 |
|
| Receivables and prepaid expenses |
|
682 |
|
|
|
663 |
|
| Total current assets |
|
7,799 |
|
|
|
10,541 |
|
| |
|
|
|
|
|
|
|
| LONG-TERM ASSETS: |
|
|
|
|
|
|
|
| Long-term assets |
|
19 |
|
|
|
18 |
|
| Property and equipment, net |
|
68 |
|
|
|
71 |
|
| Total long-term assets |
|
87 |
|
|
|
89 |
|
| |
|
|
|
|
|
|
|
| TOTAL ASSETS |
$ |
7,886 |
|
|
$ |
10,630 |
|
| |
|
|
|
|
|
|
|
| LIABILITIES AND SHAREHOLDERS' EQUITY |
|
|
|
|
|
|
|
| CURRENT LIABILITIES: |
|
|
|
|
|
|
|
| Trade payables |
$ |
543 |
|
|
$ |
700 |
|
| Other accounts payable |
|
1,075 |
|
|
|
1,231 |
|
| Total current liabilities |
|
1,618 |
|
|
|
1,931 |
|
| |
|
|
|
|
|
|
|
| |
|
|
|
|
|
|
|
| LONG-TERM LIABILITIES |
|
- |
|
|
|
- |
|
| |
|
|
|
|
|
|
|
| SHAREHOLDERS' EQUITY: |
|
|
|
|
|
|
|
| Ordinary shares of NIS 0.01 par value - 50,000,000 shares authorized
at March 31, 2017 and December 31, 2016; 16,391,770 issued and outstanding shares at March 31, 2017 and December 31, 2016 |
|
45 |
|
|
|
45 |
|
| Additional paid-in capital |
|
48,704 |
|
|
|
48,463 |
|
| Accumulated deficit |
|
(42,481 |
) |
|
|
(39,809 |
) |
| Total stockholders' equity |
|
6,268 |
|
|
|
8,699 |
|
| TOTAL LIABILITIES AND SHAREHOLDERS' EQUITY |
$ |
7,886 |
|
|
$ |
10,630 |
|
| |
|
|
|
| Bioblast Pharma Ltd. |
| |
| Consolidated Cash Flow Data |
| |
| (U.S. dollars in thousands) |
| |
| |
Three Months Ended |
| |
March 31 |
| |
|
2017 |
|
|
|
2016 |
|
| |
(Unaudited) |
|
(Unaudited) |
| Cash flows from
operating activities |
|
|
|
| Net loss |
$ |
(2,672 |
) |
|
$ |
(4,594 |
) |
| Adjustments to reconcile net loss to net cash used in operating
activities: |
|
|
|
| Depreciation and disposal of property and equipment |
|
5 |
|
|
|
6 |
|
| Share based compensation |
|
241 |
|
|
|
751 |
|
| Interest on short-term deposit |
|
(10 |
) |
|
|
(34 |
) |
| Changes in operating assets and liabilities: |
|
|
|
| Decrease (increase) in receivables and prepaid expenses |
|
(22 |
) |
|
|
338 |
|
| Decrease (increase) in long-term assets |
|
2 |
|
|
|
(25 |
) |
| Decrease in trade payables |
|
(157 |
) |
|
|
(506 |
) |
| Increase (decrease) in other accounts payable |
|
(156 |
) |
|
|
61 |
|
| Increase in long-term liabilities |
|
- |
|
|
|
55 |
|
| |
|
|
|
| Net cash used in operating activities |
|
(2,769 |
) |
|
|
(3,948 |
) |
| |
|
|
|
| Cash flow from
investing activities |
|
|
|
| |
|
|
|
| Purchase of property and equipment |
|
(2 |
) |
|
|
(8 |
) |
| Net cash used in investing activities |
|
(2 |
) |
|
|
(8 |
) |
| |
|
|
|
| Cash flow from
financing activities |
|
|
|
| |
|
|
|
| Issuance of shares and warrants, net |
|
- |
|
|
|
6,196 |
|
| Net cash provided by financing activities |
|
- |
|
|
|
6,196 |
|
| |
|
|
|
| Increase (decrease) in cash and cash equivalents |
|
(2,771 |
) |
|
|
2,240 |
|
| Cash and cash equivalents, beginning of the year |
|
6,871 |
|
|
|
7,286 |
|
| |
|
|
|
| Cash and cash equivalents, end of the year |
$ |
4,100 |
|
|
$ |
9,526 |
|
| |
|
|
|
| Supplemental Non-Cash Financing Activities: |
|
|
|
| Issuance expenses yet to be paid as of March 31,2016 |
$ |
- |
|
|
$ |
107 |
|
| |
|
|
|
| Supplemental disclosure of cash flow information: |
|
|
|
| Cash paid for taxes |
$ |
- |
|
|
$ |
104 |
|
| |
|
|
|
INVESTOR CONTACT: Matthew P. Duffy Managing Director LifeSci Advisors, LLC Telephone: 212-915-0685 Matthew@LifeSciAdvisors.com
