CAMBRIDGE, Mass., April 08, 2019 (GLOBE NEWSWIRE) -- Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in
precision genetic medicine for rare diseases, today stated that its previously announced positive clinical data from the Company’s
Limb-girdle muscular dystrophy (LGMD) Type 2E gene therapy program has been accepted for a late-breaker oral presentation at the
Muscular Dystrophy Association (MDA) Clinical and Scientific Conference in Orlando, Fla.
Title: Systemic Gene Transfer with AAVrh74.MHCK7.SGCB Increased β-sarcoglycan
Expression in Patients with Limb Girdle Muscular Dystrophy Type 2E (Rodino-Klapac et al.)
Details: Tuesday, April 16, 4:00-4:15 p.m. ET; Clinical Trials Session; Regency R-S
Louise Rodino-Klapac, Ph.D., Sarepta’s Senior Vice President of Gene Therapy, will present.
In addition to the late-breaker, six posters highlighting data from Sarepta’s RNA and gene therapy programs for
Duchenne muscular dystrophy (DMD) and LGMD 2D will be presented during the Networking & Poster Sessions in the Exhibit Hall on
Monday, April 15, and Tuesday, April 16, 2019.
The oral presentation and posters will be archived under the events and presentations section of the Sarepta
Therapeutics website at www.sarepta.com for 90 days following their presentation at MDA.
About Sarepta Therapeutics
Sarepta is at the forefront of precision genetic medicine, having built an impressive and competitive position
in Duchenne muscular dystrophy (DMD) and more recently in gene therapies for 5 Limb-girdle muscular dystrophy diseases (LGMD),
Charcot-Marie-Tooth (CMT), MPS IIIA, Pompe and other CNS-related disorders, totaling over 20 therapies in various stages of
development. The Company’s programs and research focus span several therapeutic modalities, including RNA, gene therapy and gene
editing. Sarepta is fueled by an audacious but important mission: to profoundly improve and extend the lives of patients with rare
genetic-based diseases. For more information, please visit www.sarepta.com.
Internet Posting of Information
We routinely post information that may be important to investors in the 'For Investors' section of our
website at www.sarepta.com. We encourage investors and potential investors to
consult our website regularly for important information about us.
Source: Sarepta Therapeutics, Inc.
Sarepta Therapeutics, Inc.
Investors:
Ian Estepan, 617-274-4052
iestepan@sarepta.com
Media:
Tracy Sorrentino, 617-301-8566
tsorrentino@sarepta.com
